CMI published a business research report on “Pompe Disease Therapeutic Market: Global Industry Analysis, Size, Share, Growth, Trends, and Forecasts 2021–2027”. Pompe Disease Therapeutic with 100+ market data Tables, Pie Chat, Graphs & Figures spread through Pages and easy to understand detailed analysis. The information is gathered based on modern floats and requests identified with the administrations and items.
Pompe Disease Therapeutic Market report includes historic data, present market trends, environment, technological innovation, upcoming technologies and the technical progress in the related industry. Pompe Disease Therapeutic Market offers complete, proficient report delivering market research data that is relevant for new market entrants or set up players. Key strategies of the companies operating in the market and their impact analysis have been included in the report.
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Lack of the enzyme alpha-glucosidase causes Pompe disease, which is a hereditary Lysosomal Storage Disorder (LSD) (GAA). This enables glycogen to build up in many tissues, most notably smooth muscles, skeletal muscles, and cardiac muscle. Muscle weakness, breathing difficulties, and liver and cardiac disorders are all possible side effects. Classic infantile-onset, which begins within several months of birth, non-classic infantile-onset, and adult-onset Pompe disease are the three primary forms of pompe disease, which differ in severity and emerge at various ages. Pompe illness—which often manifests by the age of one—and late-onset Pompe disease, which manifests symptoms later in childhood, teenage or adulthood. Due to the restricted range of companies who may substantially increase and develop their company potential and breadth in this industry, the global Pompe disease therapeutic market has enormous growth potential.
The expansion of the global Pompe disease treatment market is projected to be aided by increased government efforts. In light of public health concerns, the government continues to promote and advance the development of new products for the prevention, diagnosis, and treatment of uncommon diseases and disorders such as Pompe disease. In 2015, the Orphan Product Grants Program awarded 18 new grants out of 92 grant submissions, as well as financing and assistance to 67 continuing projects. Moreover, attempts by governments in countries such as Sweden, the Netherlands, and South Korea aimed at implementing compensation standards for people receiving enzyme replacement therapy (ERT) are projected to support the expansion of the global Pompe disease therapeutic market in the coming years.
The rising incidence of Pompe disease in various nations is projected to provide attractive possibilities for pharmaceutical companies to provide a customized solution for illness detection and treatment. Gene therapy and essential enzyme treatment have the potential to significantly reduce the clinical symptoms of this uncommon illness. Myozyme for the treatment of babies and children with Pompe disease and Lumizyme for late-onset non-infantile Pompe illness are the two marketed enzyme replacement therapy medicines currently available. Additionally, several pipeline medicines in phase III (Sanofi and Audentes therapies) and phase II (Biomarin) clinical trials are projected to propel the global Pompe disease therapeutic market to new heights throughout the forecast period.
Companies’ increased efforts in research and development are anticipated to drive market expansion. To meet the need for Pompe disease treatments, manufacturers are concentrating on developing new solutions by extending their pipeline. Avrobio Inc. extended their product pipeline in September 2017 by developing a gene therapy to treat Pompe disease, which uses a unique lysosomal aiming gene to provide high amounts of enzyme to lysosomes. The U.S. Food and drug Administration granted Amicus Therapeutics orphan drug designation for ATB200/AT2221 in October 2017 for the management of Pompe illness. ATB200, a recombinant human acid alpha-glucosidase enzyme with modified carbohydrate structures, notably mannose-6 phosphate to increase absorption, is co-administered with AT2221, a pharmacological chaperone, in this innovative therapy paradigm.
The high cost of therapy and the extended period of treatment, on the other hand, are limiting the expansion of the global Pompe disease therapeutic market. Lumizyme cost US$ 100,000 per year for children and US$ 300,000 per year for adult treatments in 2016, according to a Harvard School study article.
Major companies contributing in the global Pompe disease therapeutic market are Sanofi S.A., Amicus Therapeutics, Inc., Sangamo Therapeutics, Inc., Valerion Therapeutics, LLC, and Oxyrane.Sangamo Therapeutics, Inc.
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Main points in Pompe Disease Therapeutic Market Report Table of Content
Chapter 1 Industry Overview
1.3 Research Scope
1.4 Market Analysis by Regions
1.5 Pompe Disease Therapeutic Market Size Analysis from 2021 to 2027
11.6 COVID-19 Outbreak: Pompe Disease Therapeutic Industry Impact
Chapter 2 Pompe Disease Therapeutic Competition by Types, Applications, and Top Regions and Countries
2.1 Pompe Disease Therapeutic (Volume and Value) by Type
2.3 Pompe Disease Therapeutic (Volume and Value) by Regions
Chapter 3 Production Market Analysis
3.1 Production Market Analysis
3.2 Regional Production Market Analysis
Chapter 4 Pompe Disease Therapeutic Sales, Consumption, Export, Import by Regions (2016-2021)
Chapter 5 North America Pompe Disease Therapeutic Market Analysis
Chapter 6 East Asia Pompe Disease Therapeutic Market Analysis
Chapter 7 Europe Pompe Disease Therapeutic Market Analysis
Chapter 8 South Asia Pompe Disease Therapeutic Market Analysis
Chapter 9 Southeast Asia Pompe Disease Therapeutic Market Analysis
Chapter 10 Middle East Pompe Disease Therapeutic Market Analysis
Chapter 11 Africa Pompe Disease Therapeutic Market Analysis
Chapter 12 Oceania Pompe Disease Therapeutic Market Analysis
Chapter 13 South America Pompe Disease Therapeutic Market Analysis
Chapter 14 Company Profiles and Key Figures in Pompe Disease Therapeutic Business
Chapter 15 Pompe Disease Therapeutic Market Forecast (2021-2027)
Chapter 16 Conclusions
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